paperBiotech

Safety and Efficacy of Subretinal AAV-CRISPR/Cas9 Gene Editing for Rhodopsin-Mutant Retinitis Pigmentosa: A Phase I/IIa Dose-Escalation Triall

Safety and Efficacy of Subretinal AAV-CRISPR/Cas9 Gene Editing for Rhodopsin-Mutant Retinitis Pigmentosa: A Phase I/IIa Dose-Escalation Triall

publishedDate Venue Sriwijaya Journal of Ophthalmology

Source-permitted summary

Safety and Efficacy of Subretinal AAV-CRISPR/Cas9 Gene Editing for Rhodopsin-Mutant Retinitis Pigmentosa: A Phase I/IIa Dose-Escalation Triall

SourceHanif Medisiana Publisher

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Primary source
Hanif Medisiana Publisher
Correction status
none
Evidence coverage
1 sources / 1 publishers
Last metadata check
Jul 19, 2026
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AI Reading Notes

Core signal

Structured notes generated from source-linked AISci metadata. Treat them as a reading aid, not a substitute for the paper.

Core signal
Safety and Efficacy of Subretinal AAV-CRISPR/Cas9 Gene Editing for Rhodopsin-Mutant Retinitis Pigmentosa: A Phase I/IIa Dose-Escalation Triall
Field context
Genomics and Gene Editing
People and labs
Not stated in the reviewed source.
Why it matters
Recent source-backed research output for AISci Stage A browsing.
Limits to check
AISci rank score does not assess scientific quality or citation impact.

Publication facts

Venue
Sriwijaya Journal of OphthalmologySourceHanif Medisiana Publisher

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  1. paperSafety and Efficacy of Subretinal AAV-CRISPR/Cas9 Gene Editing for Rhodopsin-Mutant Retinitis Pigmentosa: A Phase I/IIa Dose-Escalation Triall